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Metabolic Diseases

Treatments for inborn errors of metabolism, lysosomal storage disorders, and other metabolic conditions.

Companies
0
Pipeline Drugs
301
Key People
535

Metabolic Diseases Pipeline (301 drugs)

Commercial: 64Approved: 32Phase 2: 32Preclinical: 27Phase 3: 25Phase 1: 18Pre-clinical: 14Phase 1/2: 13Not Specified: 7Research: 6Discovery/Preclinical: 5Discovery: 5Pre-clinical Tool: 5Phase II: 4Various: 4Phase 2b: 3Pre-Clinical: 3Not Disclosed: 3Platform/Tool Development: 3IND-Enabling: 2Preclinical/Phase 1: 2R&D: 2Various (Typically Phase 2-4): 2Acquisition: 1Filed: 1Phase III: 1Regulatory Review: 1Phase 3 / Commercial: 1Non-GMP / Research: 1Discovery to Preclinical: 1Clinical Development: 1Phase 2/3: 1Phase 3-ready: 1Phase 3 (likely): 1Phase 1/Phase 2 (implied): 1Pivotal: 1Phase 2a: 1Not Specified (Likely Phase 3/NDA): 1Commercial Tool: 1Service Offering: 1Various (Typically Phase 3): 1Approved/Commercial: 1Research Use Only: 1
DrugCompanyIndicationPhase
BGE-102BioAge LabsCardiovascular Risk and Metabolic DysfunctionPhase 1
APJ ProgramBioAge LabsObesityPreclinical
Tagrisso (osimertinib)AstraZenecaEGFR-mutated lung cancerApproved
Imfinzi (durvalumab)AstraZenecaVarious cancersApproved
Lynparza (olaparib)AstraZenecaBRCA-mutated cancersApproved
Calquence (acalabrutinib)AstraZenecaBlood cancersApproved
Farxiga (dapagliflozin)AstraZenecaDiabetes/Heart failure/CKDApproved
Brilinta (ticagrelor)AstraZenecaCardiovascular diseaseApproved
SymbicortAstraZenecaAsthma/COPDApproved
BreztriAstraZenecaCOPDApproved
ForxigaAstraZenecaType 2 diabetesApproved
Crestor (rosuvastatin)AstraZenecaHigh cholesterolApproved
CosentyxยฎNovartisPediatric Hidradenitis Suppurativa (12+)Approved
Pan-mutant-selective PI3Kฮฑ inhibitorNovartisBreast CancerAcquisition
Mitoxantrone LiposomeCSPC Pharmaceutical Group LimitedVarious CancersPhase 3
Doxorubicin LiposomeCSPC Pharmaceutical Group LimitedOvarian CancerPhase 3
Alemtuzumab BiosimilarCSPC Pharmaceutical Group LimitedHematologic MalignanciesPhase 3
CSPC-DM02CSPC Pharmaceutical Group LimitedSolid TumorsPhase 2
NBP (Butylphthalide)CSPC Pharmaceutical Group LimitedStrokeCommercial
Caffeine CitrateCSPC Pharmaceutical Group LimitedNeonatal ApneaCommercial
Vitamin D AnalogsCSPC Pharmaceutical Group LimitedChronic Kidney DiseaseCommercial
ResmetiromMadrigal PharmaceuticalsMASH with moderate to advanced fibrosis (F2-F3)Approved
Ervogastat combinationMadrigal PharmaceuticalsMASHPhase 2
MGL-2086Madrigal PharmaceuticalsUndisclosedPhase 1
Cardiovascular PortfolioShenzhen Salubris PharmaceuticalsHypertension and Heart DiseaseCommercial
Respiratory ProductsShenzhen Salubris PharmaceuticalsRespiratory DisordersCommercial
Metabolic Disease ProductsShenzhen Salubris PharmaceuticalsDiabetes and Metabolic DisordersCommercial
Generic Drug PortfolioShenzhen Salubris PharmaceuticalsVarious Therapeutic AreasCommercial
Medical Device ProductsShenzhen Salubris PharmaceuticalsDiagnostic and Therapeutic ApplicationsCommercial
Rusfertide (PTG-300)Protagonist TherapeuticsPolycythemia VeraPhase 3
Icotrokinra (JNJ-2113)Protagonist TherapeuticsModerate-to-Severe PsoriasisPhase 3
PN-881Protagonist TherapeuticsPsoriasis, Psoriatic Arthritis, Hidradenitis Suppurativa, SpondyloarthritisPhase 1
PN-477scProtagonist TherapeuticsObesity & Associated Co-MorbiditiesIND-Enabling
PN-477oralProtagonist TherapeuticsObesity & Associated Co-MorbiditiesIND-Enabling
Oral HepcidinProtagonist TherapeuticsPolycythemia Vera, Hereditary HemochromatosisPre-clinical
Tinlarebant (LBS-008)Belite BioGeographic Atrophy (Dry AMD)Phase 3
LBS-009Belite BioNon-Fatty Liver DiseasePreclinical
Leclaza (Lazertinib)YuhanEGFR T790M-mutated Non-Small Cell Lung Cancer (NSCLC)Approved
Jentadueto (Linagliptin/Metformin)YuhanType 2 DiabetesApproved
Nesina (Alogliptin)YuhanType 2 DiabetesApproved
YH25448 (Gumarontinib)YuhanEGFR Exon20 Insertion+ NSCLCPhase 3
YH32367YuhanHER2-positive Solid TumorsPhase 1/2
YH29407YuhanMultiple MyelomaPhase 1
YH003YuhanSolid Tumors (e.g., Pancreatic Cancer)Phase 2
YH001YuhanSolid TumorsPhase 2
YH14618YuhanMetabolic Dysfunction-Associated Steatohepatitis (MASH)Phase 1
YH25724YuhanFibrotic DiseasesPreclinical/Phase 1
Chemical Generics PortfolioChina Resources Pharmaceutical GroupVarious (Cardiovascular, CNS, Anti-infective)Approved
Traditional Chinese Medicine PortfolioChina Resources Pharmaceutical GroupVarious Chronic Diseases & WellnessApproved
Biosimilar CandidatesChina Resources Pharmaceutical GroupOncology, Autoimmune DiseasesPhase 3