🧬Rare & Orphan Diseases

Market Cap$299.7B
1D+1.32%
Companies239
Public Cos73

SECTOR MARKET CAP

$299.7B+255.7%ALL

TOP COMPANIES

#CompanyCountryValuationTicker
1
Roivant Sciences
Roivant Sciences
United Kingdom$22.7BROIV
2
United Therapeutics
United Therapeutics
United States$22.7BUTHR
3
Insmed
Insmed
United States$21.6BINSM
4
Swedish Orphan Biovitrum
Swedish Orphan Biovitrum
Sweden$16.1BSOBI.ST
5
Ascendis Pharma
Ascendis Pharma
Denmark$15.3BASND
6
Ipsen
Ipsen
France$14.7BIPN.PA
7
Jazz Pharmaceuticals
Jazz Pharmaceuticals
Ireland$14.1BJAZZ
8
BridgeBio Pharma
BridgeBio Pharma
United States$13.2BBBIO
9
PharmaEssentia
PharmaEssentia
Taiwan$12.9B6446.TW
10
Ionis Pharmaceuticals
Ionis Pharmaceuticals
United States$12.4BIONS
11
Recordati
Recordati
Italy$11.9BREC.MI
12
Arrowhead Pharmaceuticals
Arrowhead Pharmaceuticals
United States$11.7BARWR
13
BioMarin Pharmaceutical
BioMarin Pharmaceutical
United States$10.8BBMRN
14
Krystal Biotech
Krystal Biotech
United States$10.4BKRYS
15
Praxis Precision Medicines
Praxis Precision Medicines
United States$8.3BPRAX
16
Kyowa Kirin
Kyowa Kirin
Japan$8.2B4151.T
17
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals
United States$6.8BRYTM
18
PTC Therapeutics
PTC Therapeutics
United States$6.7BPTCT
19
Mirum Pharmaceuticals
Mirum Pharmaceuticals
United States$6.7BMIRM
20
Liquidia
Liquidia
United States$6.6BLQDA

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