๐ŸงฌRare & Orphan Diseases

Market Cap$335.6B
1D-1.59%
Companies239
Public Cos59

SECTOR MARKET CAP

$335.6B+298.3%ALL

TOP COMPANIES

#CompanyCountryValuationTicker
1
Takeda Pharmaceutical
Takeda Pharmaceutical
Japan$56.3BTAK
2
Insmed
Insmed
United States$29.3BINSM
3
United Therapeutics
United Therapeutics
United States$23.0BUTHR
4
Roivant Sciences
Roivant Sciences
United Kingdom$19.8BROIV
5
Ipsen
Ipsen
France$14.2BIPN.PA
6
Ascendis Pharma
Ascendis Pharma
Denmark$13.6BASND
7
Swedish Orphan Biovitrum
Swedish Orphan Biovitrum
Sweden$13.3BSOBI.ST
8
BridgeBio Pharma
BridgeBio Pharma
United States$13.3BBBIO
9
Ionis Pharmaceuticals
Ionis Pharmaceuticals
United States$11.7BIONS
10
Jazz Pharmaceuticals
Jazz Pharmaceuticals
Ireland$11.1BJAZZ
11
Recordati
Recordati
Italy$10.5BREC.MI
12
BioMarin Pharmaceutical
BioMarin Pharmaceutical
United States$10.4BBMRN
13
Praxis Precision Medicines
Praxis Precision Medicines
United States$8.3BPRAX
14
Arrowhead Pharmaceuticals
Arrowhead Pharmaceuticals
United States$7.9BARWR
15
Kyowa Kirin
Kyowa Kirin
Japan$7.7B4151.T
16
PharmaEssentia
PharmaEssentia
Taiwan$7.4B6446.TW
17
Krystal Biotech
Krystal Biotech
United States$7.4BKRYS
18
Belite Bio
Belite Bio
United States$6.1BBLTE
19
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals
United States$6.0BRYTM
20
Cogent Biosciences
Cogent Biosciences
United States$5.4BCOGT