🧬Rare & Orphan Diseases

Market Cap$292.2B
1D-0.34%
Companies239
Public Cos75

SECTOR MARKET CAP

$292.2B+246.8%ALL

TOP COMPANIES

#CompanyCountryValuationTicker
1
United Therapeutics
United Therapeutics
United States$24.2BUTHR
2
Insmed
Insmed
United States$22.8BINSM
3
Roivant Sciences
Roivant Sciences
United Kingdom$20.3BROIV
4
Swedish Orphan Biovitrum
Swedish Orphan Biovitrum
Sweden$16.5BSOBI.ST
5
Ipsen
Ipsen
France$16.2BIPN.PA
6
Ascendis Pharma
Ascendis Pharma
Denmark$15.3BASND
7
Jazz Pharmaceuticals
Jazz Pharmaceuticals
Ireland$14.2BJAZZ
8
BridgeBio Pharma
BridgeBio Pharma
United States$13.1BBBIO
9
Ionis Pharmaceuticals
Ionis Pharmaceuticals
United States$12.7BIONS
10
Recordati
Recordati
Italy$12.0BREC.MI
11
Arrowhead Pharmaceuticals
Arrowhead Pharmaceuticals
United States$10.7BARWR
12
BioMarin Pharmaceutical
BioMarin Pharmaceutical
United States$10.5BBMRN
13
Praxis Precision Medicines
Praxis Precision Medicines
United States$9.3BPRAX
14
Krystal Biotech
Krystal Biotech
United States$8.8BKRYS
15
PharmaEssentia
PharmaEssentia
Taiwan$8.6B6446.TW
16
Kyowa Kirin
Kyowa Kirin
Japan$7.8B4151.T
17
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals
United States$6.5BRYTM
18
Mirum Pharmaceuticals
Mirum Pharmaceuticals
United States$6.5BMIRM
19
Belite Bio
Belite Bio
United States$6.2BBLTE
20
Cogent Biosciences
Cogent Biosciences
United States$6.0BCOGT

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