TSHA-101

Phase 1/2Active
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Interest: 30/100
30
Hype Score

Development Stage

Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Infantile GM2 Gangliosidosis (Disorder)

Conditions

Infantile GM2 Gangliosidosis (Disorder)

Trial Timeline

Mar 12, 2021 → Mar 12, 2027

About TSHA-101

TSHA-101 is a phase 1/2 stage product being developed by Taysha Gene Therapies for Infantile GM2 Gangliosidosis (Disorder). The current trial status is active. This product is registered under clinical trial identifier NCT04798235. Target conditions include Infantile GM2 Gangliosidosis (Disorder).

What happened to similar drugs?

3 of 7 similar drugs in Infantile GM2 Gangliosidosis (Disorder) were approved

Approved (3) Terminated (2) Active (4)
VigabatrinLundbeckApproved
🔄GWP42003-PJazz PharmaceuticalsPhase 3
🔄GWP42003-PJazz PharmaceuticalsPhase 3
🔄Cholic AcidsMirum PharmaceuticalsPhase 3
🔄Cipaglucosidase alfa + MiglustatAmicus TherapeuticsPhase 3

Hype Score Breakdown

Clinical
9
Activity
12
Company
9
Novelty
0
Community
0

Clinical Trials (1)

NCT IDPhaseStatus
NCT04798235Phase 1/2Active

Competing Products

16 competing products in Infantile GM2 Gangliosidosis (Disorder)

See all competitors
ProductCompanyStageHype Score
MAS825 + PlaceboNovartisPhase 2
39
alglucosidase alfa + alglucosidase alfaSanofiApproved
35
MyozymeSanofiPhase 2
35
Bacillus Clausii Multi ATB Resist + PlaceboSanofiApproved
43
RadiprodilUCBPhase 2
27
Larotrectinib (Vitrakvi, BAY2757556) + Standard of CareBayerPre-clinical
23
Sabril®LundbeckPre-clinical
23
VigabatrinLundbeckApproved
32
NusinersenBiogenPre-clinical
23
GWP42003-PJazz PharmaceuticalsPhase 3
37
GWP42003-PJazz PharmaceuticalsPhase 3
37
Cerliponase AlfaBioMarin PharmaceuticalPre-clinical
27
Cholic AcidsMirum PharmaceuticalsPhase 3
37
Cipaglucosidase alfa + MiglustatAmicus TherapeuticsPhase 3
44
ATB200 + AT2221Amicus TherapeuticsPre-clinical
27
RP-L401Rocket PharmaceuticalsPhase 1
11