Cerliponase Alfa

Pre-clinicalActive
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20
Hype Score

Development Stage

1
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2

Conditions

Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2

Trial Timeline

Aug 19, 2020 โ†’ Aug 31, 2030

About Cerliponase Alfa

Cerliponase Alfa is a pre-clinical stage product being developed by BioMarin Pharmaceutical for Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2. The current trial status is active. This product is registered under clinical trial identifier NCT04476862. Target conditions include Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2.

Hype Score Breakdown

Clinical
5
Activity
2
Company
7
Novelty
2
Community
1

Clinical Trials (1)

NCT IDPhaseStatus
NCT04476862Pre-clinicalActive