RP-L401
Phase 1Terminated 0 watching 0 views this week๐ค Quiet
25
Development Stage
โ
Pre-clinical2
Phase 13
Phase 24
Phase 35
ApprovedIndication / Disease
Infantile Malignant Osteopetrosis
Conditions
Infantile Malignant Osteopetrosis
Trial Timeline
Nov 19, 2020 โ May 21, 2021
NCT ID
NCT04525352About RP-L401
RP-L401 is a phase 1 stage product being developed by Rocket Pharmaceuticals for Infantile Malignant Osteopetrosis. The current trial status is terminated. This product is registered under clinical trial identifier NCT04525352. Target conditions include Infantile Malignant Osteopetrosis.
Hype Score Breakdown
Clinical
10
Activity
5
Company
2
Novelty
3
Community
2
Clinical Trials (1)
| NCT ID | Phase | Status |
|---|---|---|
| NCT04525352 | Phase 1 | Terminated |
Competing Products
16 competing products in Infantile Malignant Osteopetrosis
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| TSHA-101 | Taysha Gene Therapies | Phase 1/2 | 36 |
| MAS825 + Placebo | Novartis | Phase 2 | 52 |
| alglucosidase alfa + alglucosidase alfa | Sanofi | Approved | 84 |
| Myozyme | Sanofi | Phase 2 | 51 |
| Bacillus Clausii Multi ATB Resist + Placebo | Sanofi | Approved | 84 |
| Radiprodil | UCB | Phase 2 | 49 |
| Larotrectinib (Vitrakvi, BAY2757556) + Standard of Care | Bayer | Pre-clinical | 20 |
| Sabrilยฎ | Lundbeck | Pre-clinical | 20 |
| Vigabatrin | Lundbeck | Approved | 82 |
| Nusinersen | Biogen | Pre-clinical | 20 |
| GWP42003-P | Jazz Pharmaceuticals | Phase 3 | 74 |
| GWP42003-P | Jazz Pharmaceuticals | Phase 3 | 74 |
| Cerliponase Alfa | BioMarin Pharmaceutical | Pre-clinical | 20 |
| Cholic Acids | Mirum Pharmaceuticals | Phase 3 | 74 |
| Cipaglucosidase alfa + Miglustat | Amicus Therapeutics | Phase 3 | 74 |
| ATB200 + AT2221 | Amicus Therapeutics | Pre-clinical | 20 |