Myozyme

Phase 2Completed
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51
Hype Score

Development Stage

Pre-clinical
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Pompe Disease Infantile-Onset

Conditions

Pompe Disease Infantile-Onset, Glycogen Storage Disease Type II

Trial Timeline

Apr 1, 2003 → Jul 1, 2006

About Myozyme

Myozyme is a phase 2 stage product being developed by Sanofi for Pompe Disease Infantile-Onset. The current trial status is completed. This product is registered under clinical trial identifier NCT00763932. Target conditions include Pompe Disease Infantile-Onset, Glycogen Storage Disease Type II.

Hype Score Breakdown

Clinical
17
Activity
12
Company
9
Novelty
5
Community
5

Clinical Trials (8)

NCT IDPhaseStatus
NCT00268944Phase 3Completed
NCT00125879Phase 2/3Completed
NCT00250939Phase 2Completed
NCT00074932Pre-clinicalCompleted
NCT00059280Phase 2/3Completed
NCT00765414Phase 2Completed
NCT00763932Phase 2Completed
NCT00053573Phase 1/2Completed

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