Infantile GM2 Gangliosidosis (Disorder)
1 competing product in clinical development for Infantile GM2 Gangliosidosis (Disorder).
Pipeline by Phase
Phase 1/21
All Products (1)
| Product | Company | Stage | Status | Hype |
|---|---|---|---|---|
| TSHA-101 | Taysha Gene Therapies | Phase 1/2 | Active | 36 |