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Focus Area Program

Duchenne Muscular Dystrophy (DMD)

Not SpecifiedCore Focus Area

Key Facts

Indication
Duchenne Muscular Dystrophy (DMD)
Phase
Not Specified
Status
Core Focus Area
Company

About Santhera Pharmaceuticals

Santhera Pharmaceuticals is a Swiss public company with a focused mission to develop and commercialize treatments for rare neuromuscular diseases, exemplified by its long-term dedication to Duchenne muscular dystrophy (DMD). The company's strategy centers on identifying and advancing compounds that address specific pathological mechanisms in these high-need areas. While historically involved with the FDA-approved drug vamorolone for DMD, Santhera's current pipeline and strategic direction emphasize its ongoing commitment to this challenging therapeutic space.

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Other Duchenne Muscular Dystrophy (DMD) Drugs

DrugCompanyPhase
DT-DEC01Dystrogen TherapeuticsPhase 1
Skeletal Muscle Regeneration ProgramIPS HEARTPre-clinical
KYMBEE (deflazacort)Upsher-SmithApproved
ALY688ERAllysta PharmaceuticalsPhase 1
AVGN7 + AVGNDAAVogenPre-clinical
Myomatrix Stabilization ProgramStrykagenPreclinical
RIPPLE™ (implied)SonoTheraPreclinical
Vamorolone (AGAMREE)ReveraGen BioPharmaApproved
RGX-202ReGenX BiosciencesPhase 1/2
AGAMREE (vamorolone)Catalyst PharmaceuticalsMarketed
EDG-5506Edgewise TherapeuticsPhase 2
ELEVIDYS (delandistrogene moxeparvovec-rokl)Sarepta TherapeuticsMarketed / Phase 3