Home/Pipeline/AGAMREE (vamorolone)

AGAMREE (vamorolone)

Duchenne Muscular Dystrophy (DMD)

MarketedCommercial; Long-term safety monitored via SUMMIT RegistryDMD-001 (SUMMIT)

Key Facts

Indication
Duchenne Muscular Dystrophy (DMD)
Phase
Marketed
Status
Commercial; Long-term safety monitored via SUMMIT Registry
Company

About Catalyst Pharmaceuticals

Catalyst Pharmaceuticals has successfully transitioned from a development-stage entity to a profitable commercial organization focused on rare neuromuscular and neurological diseases. Its strategy centers on acquiring or in-licensing late-stage/commercial assets, maximizing lifecycle value, and maintaining an intense patient-first operational culture. This approach has yielded a marketed portfolio, a growing pipeline, and recognition as a top small-cap company, positioning it for continued growth in specialized therapeutic areas.

View full company profile

About Catalyst Pharmaceuticals

Catalyst Pharmaceuticals has successfully transitioned from a development-stage entity to a profitable commercial organization focused on rare neuromuscular and neurological diseases. Its strategy centers on acquiring or in-licensing late-stage/commercial assets, maximizing lifecycle value, and maintaining an intense patient-first operational culture. This approach has yielded a marketed portfolio, a growing pipeline, and recognition as a top small-cap company, positioning it for continued growth in specialized therapeutic areas.

View full company profile

Other Duchenne Muscular Dystrophy (DMD) Drugs