REGN7999 + Placebo

Phase 2Recruiting
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51
Hype Score

Development Stage

Pre-clinical
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Non-Transfusion Dependent Beta-Thalassemia (NTDT)

Conditions

Non-Transfusion Dependent Beta-Thalassemia (NTDT)

Trial Timeline

Sep 30, 2024 → Jan 24, 2028

About REGN7999 + Placebo

REGN7999 + Placebo is a phase 2 stage product being developed by Regeneron Pharmaceuticals for Non-Transfusion Dependent Beta-Thalassemia (NTDT). The current trial status is recruiting. This product is registered under clinical trial identifier NCT06421636. Target conditions include Non-Transfusion Dependent Beta-Thalassemia (NTDT).

Hype Score Breakdown

Clinical
17
Activity
12
Company
9
Novelty
5
Community
5

Clinical Trials (2)

NCT IDPhaseStatus
NCT06421636Phase 2Recruiting
NCT05481333Phase 1Completed

Competing Products

5 competing products in Non-Transfusion Dependent Beta-Thalassemia (NTDT)

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ProductCompanyStageHype Score
deferasirox + placeboNovartisPhase 2
52
deferasiroxNovartisApproved
85
Placebo Matching Mitapivat + MitapivatAgios PharmaceuticalsPhase 3
72
SLN124 + PlaceboSilence TherapeuticsPhase 1
25
SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as PlaceboSilence TherapeuticsPhase 1
25