SLN124 + Placebo

Phase 1Completed
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Interest: 19/100
19
Hype Score

Development Stage

Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Non-transfusion-dependent Thalassemia

Conditions

Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome

Trial Timeline

Apr 14, 2021 → May 23, 2023

About SLN124 + Placebo

SLN124 + Placebo is a phase 1 stage product being developed by Silence Therapeutics for Non-transfusion-dependent Thalassemia. The current trial status is completed. This product is registered under clinical trial identifier NCT04718844. Target conditions include Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome.

What happened to similar drugs?

0 of 1 similar drugs in Non-transfusion-dependent Thalassemia were approved

Approved (0) Terminated (0) Active (1)
🔄Placebo Matching Mitapivat + MitapivatAgios PharmaceuticalsPhase 3

Hype Score Breakdown

Clinical
6
Activity
8
Company
5
Novelty
0
Community
0

Clinical Trials (3)

NCT IDPhaseStatus
NCT05499013Phase 1/2Active
NCT04718844Phase 1Completed
NCT04559971Phase 1Completed

Competing Products

2 competing products in Non-transfusion-dependent Thalassemia

See all competitors