SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as Placebo

Phase 1Withdrawn
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Interest: 11/100
11
Hype Score

Development Stage

Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Non-transfusion-dependent Thalassemia

Conditions

Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome

Trial Timeline

Aug 20, 2019 → Oct 14, 2021

About SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as Placebo

SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as Placebo is a phase 1 stage product being developed by Silence Therapeutics for Non-transfusion-dependent Thalassemia. The current trial status is withdrawn. This product is registered under clinical trial identifier NCT04176653. Target conditions include Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome.

What happened to similar drugs?

0 of 1 similar drugs in Non-transfusion-dependent Thalassemia were approved

Approved (0) Terminated (0) Active (1)
🔄Placebo Matching Mitapivat + MitapivatAgios PharmaceuticalsPhase 3

Hype Score Breakdown

Clinical
6
Activity
0
Company
5
Novelty
0
Community
0

Clinical Trials (1)

NCT IDPhaseStatus
NCT04176653Phase 1Withdrawn

Competing Products

2 competing products in Non-transfusion-dependent Thalassemia

See all competitors
ProductCompanyStageHype Score
Placebo Matching Mitapivat + MitapivatAgios PharmaceuticalsPhase 3
38
SLN124 + PlaceboSilence TherapeuticsPhase 1
19