Placebo Matching Mitapivat + Mitapivat

Phase 3Active
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72
Hype Score

Development Stage

โœ“
Pre-clinical
โœ“
Phase 1
โœ“
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Non-Transfusion-dependent Alpha-Thalassemia

Conditions

Non-Transfusion-dependent Alpha-Thalassemia, Non-Transfusion-dependent Beta-Thalassemia

Trial Timeline

Dec 20, 2021 โ†’ Dec 1, 2028

About Placebo Matching Mitapivat + Mitapivat

Placebo Matching Mitapivat + Mitapivat is a phase 3 stage product being developed by Agios Pharmaceuticals for Non-Transfusion-dependent Alpha-Thalassemia. The current trial status is active. This product is registered under clinical trial identifier NCT04770753. Target conditions include Non-Transfusion-dependent Alpha-Thalassemia, Non-Transfusion-dependent Beta-Thalassemia.

Hype Score Breakdown

Clinical
27
Activity
18
Company
5
Novelty
9
Community
10

Clinical Trials (2)

NCT IDPhaseStatus
NCT04770753Phase 3Active
NCT04770779Phase 3Active

Competing Products

2 competing products in Non-Transfusion-dependent Alpha-Thalassemia

See all competitors
ProductCompanyStageHype Score
SLN124 + PlaceboSilence TherapeuticsPhase 1
25
SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as PlaceboSilence TherapeuticsPhase 1
25