Single intravenous (IV) dose of human Low Density Lipoprotein Receptor (LDLR) Gene Therapy

Pre-clinicalUNKNOWN
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Interest: 12/100
12
Hype Score

Development Stage

1
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Homozygous Familial Hypercholesterolemia (HoFH)

Conditions

Homozygous Familial Hypercholesterolemia (HoFH)

Trial Timeline

Sep 30, 2019 → Sep 29, 2025

About Single intravenous (IV) dose of human Low Density Lipoprotein Receptor (LDLR) Gene Therapy

Single intravenous (IV) dose of human Low Density Lipoprotein Receptor (LDLR) Gene Therapy is a pre-clinical stage product being developed by REGENXBIO for Homozygous Familial Hypercholesterolemia (HoFH). The current trial status is unknown. This product is registered under clinical trial identifier NCT04080050. Target conditions include Homozygous Familial Hypercholesterolemia (HoFH).

What happened to similar drugs?

1 of 17 similar drugs in Homozygous Familial Hypercholesterolemia (HoFH) were approved

Approved (1) Terminated (0) Active (16)
🔄Rosuvastatin 20mg + PlaceboAstraZenecaPhase 3
🔄Rosuvastatin 20mgAstraZenecaPhase 3
🔄Inclisiran + PlaceboNovartisPhase 3
🔄InclisiranNovartisPhase 3
🔄Inclisiran + PlaceboNovartisPhase 3
evolocumabAmgenApproved

Hype Score Breakdown

Clinical
3
Activity
4
Company
5
Novelty
0
Community
0

Clinical Trials (1)

NCT IDPhaseStatus
NCT04080050Pre-clinicalUNKNOWN

Competing Products

20 competing products in Homozygous Familial Hypercholesterolemia (HoFH)

See all competitors
ProductCompanyStageHype Score
Rosuvastatin 20mg + PlaceboAstraZenecaPhase 3
40
Rosuvastatin 20mgAstraZenecaPhase 3
40
Inclisiran + PlaceboNovartisPhase 3
40
Inclisiran Sodium for injection + Placebo + PlacebosNovartisPhase 3
40
InclisiranNovartisPhase 3
44
INC280 + BuparlisibNovartisPhase 1/2
24
Inclisiran + PlaceboNovartisPhase 3
47
Evolocumab + PlaceboAmgenPhase 2/3
38
evolocumabAmgenApproved
43
MBX-8025 50 mg (Dose Escalation Period 1) + MBX-8025 50 mg or 100 mg (Dose Escalation Period 2) + MBX-8025 50 mg, 100 mg or 200 mg (Dose Escalation Period 3)Gilead SciencesPhase 2
35
IBI306 + IBI306Innovent BiologicsPhase 2/3
38
BMS-986504 + [14C]-BMS-986504Bristol Myers SquibbPhase 1
36
Lumacaftor Plus Ivacaftor Combination + Ivacaftor + PlaceboVertex PharmaceuticalsPhase 3
40
Placebo + Lumacaftor Plus Ivacaftor Combination + IvacaftorVertex PharmaceuticalsPhase 3
40
Lumacaftor Plus Ivacaftor Combination + IvacaftorVertex PharmaceuticalsPhase 3
40
Alirocumab + PlaceboSanofiPhase 3
40
AK102 + Statins + EzetimibeAkesoPhase 2
35
EvinacumabRegeneron PharmaceuticalsPhase 3
40
evinacumabRegeneron PharmaceuticalsPhase 3
40
REGN1500 250 mg SC/15 mg/kg IV/450 mg SCRegeneron PharmaceuticalsPhase 2
35