RP-L301

Phase 1Completed
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25
Hype Score

Development Stage

โœ“
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Pyruvate Kinase Deficiency

Conditions

Pyruvate Kinase Deficiency

Trial Timeline

Jul 6, 2020 โ†’ Jun 9, 2025

About RP-L301

RP-L301 is a phase 1 stage product being developed by Rocket Pharmaceuticals for Pyruvate Kinase Deficiency. The current trial status is completed. This product is registered under clinical trial identifier NCT04105166. Target conditions include Pyruvate Kinase Deficiency.

Hype Score Breakdown

Clinical
10
Activity
5
Company
2
Novelty
3
Community
2

Clinical Trials (2)

NCT IDPhaseStatus
NCT06422351Phase 2Recruiting
NCT04105166Phase 1Completed

Competing Products

9 competing products in Pyruvate Kinase Deficiency

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ProductCompanyStageHype Score
TriheptanoinUltragenyx PharmaceuticalPhase 1
28
Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
72
Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
72
MitapivatAgios PharmaceuticalsPhase 3
72
Placebo + AG-348Agios PharmaceuticalsPhase 3
72
MitapivatAgios PharmaceuticalsApproved
80
AG-348Agios PharmaceuticalsPhase 3
72
AG-348Agios PharmaceuticalsPhase 2
47
RP-L301Rocket PharmaceuticalsPhase 2
44