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RP-L301

Phase 1Completed
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Interest: 19/100
19
Hype Score

Development Stage

✓
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Pyruvate Kinase Deficiency

Conditions

Pyruvate Kinase Deficiency

Trial Timeline

Jul 6, 2020 → Jun 9, 2025

NCT ID
NCT04105166

About RP-L301

RP-L301 is a phase 1 stage product being developed by Rocket Pharmaceuticals for Pyruvate Kinase Deficiency. The current trial status is completed. This product is registered under clinical trial identifier NCT04105166. Target conditions include Pyruvate Kinase Deficiency.

What happened to similar drugs?

1 of 6 similar drugs in Pyruvate Kinase Deficiency were approved

Approved (1) Terminated (0) Active (5)
✅MitapivatAgios PharmaceuticalsApproved
🔄Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
🔄Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
🔄MitapivatAgios PharmaceuticalsPhase 3
🔄Placebo + AG-348Agios PharmaceuticalsPhase 3
🔄AG-348Agios PharmaceuticalsPhase 3

Hype Score Breakdown

Clinical
6
Activity
8
Company
5
Novelty
0
Community
0

Clinical Trials (2)

NCT IDPhaseStatus
NCT06422351Phase 2Recruiting
NCT04105166Phase 1Completed

Competing Products

9 competing products in Pyruvate Kinase Deficiency

See all competitors
ProductCompanyStageHype Score
TriheptanoinUltragenyx PharmaceuticalPhase 1
30
Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
38
Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
38
MitapivatAgios PharmaceuticalsPhase 3
34
Placebo + AG-348Agios PharmaceuticalsPhase 3
34
MitapivatAgios PharmaceuticalsApproved
44
AG-348Agios PharmaceuticalsPhase 3
34
AG-348Agios PharmaceuticalsPhase 2
29
RP-L301Rocket PharmaceuticalsPhase 2
32