Placebo + AG-348

Phase 3Completed
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72
Hype Score

Development Stage

โœ“
Pre-clinical
โœ“
Phase 1
โœ“
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Pyruvate Kinase Deficiency

Conditions

Pyruvate Kinase Deficiency, Anemia, Hemolytic

Trial Timeline

Aug 9, 2018 โ†’ Oct 9, 2020

About Placebo + AG-348

Placebo + AG-348 is a phase 3 stage product being developed by Agios Pharmaceuticals for Pyruvate Kinase Deficiency. The current trial status is completed. This product is registered under clinical trial identifier NCT03548220. Target conditions include Pyruvate Kinase Deficiency, Anemia, Hemolytic.

Hype Score Breakdown

Clinical
27
Activity
18
Company
5
Novelty
9
Community
10

Clinical Trials (1)

NCT IDPhaseStatus
NCT03548220Phase 3Completed

Competing Products

9 competing products in Pyruvate Kinase Deficiency

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TriheptanoinUltragenyx PharmaceuticalPhase 1
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Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
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Mitapivat + Mitapivat-matching placeboAgios PharmaceuticalsPhase 3
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MitapivatAgios PharmaceuticalsPhase 3
72
MitapivatAgios PharmaceuticalsApproved
80
AG-348Agios PharmaceuticalsPhase 3
72
AG-348Agios PharmaceuticalsPhase 2
47
RP-L301Rocket PharmaceuticalsPhase 1
25
RP-L301Rocket PharmaceuticalsPhase 2
44