Mitapivat
ApprovedRecruiting 0 watching 0 views this week๐ฅ Hot
80
Development Stage
โ
Pre-clinicalโ
Phase 1โ
Phase 2โ
Phase 35
ApprovedIndication / Disease
Pyruvate Kinase Deficiency
Conditions
Pyruvate Kinase Deficiency, Anemia, Hemolytic
Trial Timeline
Jul 6, 2023 โ Aug 1, 2029
NCT ID
NCT05777993About Mitapivat
Mitapivat is a approved stage product being developed by Agios Pharmaceuticals for Pyruvate Kinase Deficiency. The current trial status is recruiting. This product is registered under clinical trial identifier NCT05777993. Target conditions include Pyruvate Kinase Deficiency, Anemia, Hemolytic.
Hype Score Breakdown
Clinical
30
Activity
20
Company
5
Novelty
10
Community
12
Clinical Trials (6)
| NCT ID | Phase | Status |
|---|---|---|
| NCT06286046 | Phase 2 | Recruiting |
| NCT07055243 | Phase 2 | Recruiting |
| NCT05777993 | Approved | Recruiting |
| NCT05610657 | Phase 1 | Completed |
| NCT05031780 | Phase 2/3 | Active |
| NCT03853798 | Phase 3 | Completed |
Competing Products
9 competing products in Pyruvate Kinase Deficiency
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| Triheptanoin | Ultragenyx Pharmaceutical | Phase 1 | 28 |
| Mitapivat + Mitapivat-matching placebo | Agios Pharmaceuticals | Phase 3 | 72 |
| Mitapivat + Mitapivat-matching placebo | Agios Pharmaceuticals | Phase 3 | 72 |
| Mitapivat | Agios Pharmaceuticals | Phase 3 | 72 |
| Placebo + AG-348 | Agios Pharmaceuticals | Phase 3 | 72 |
| AG-348 | Agios Pharmaceuticals | Phase 3 | 72 |
| AG-348 | Agios Pharmaceuticals | Phase 2 | 47 |
| RP-L301 | Rocket Pharmaceuticals | Phase 1 | 25 |
| RP-L301 | Rocket Pharmaceuticals | Phase 2 | 44 |