Mitapivat
ApprovedRecruiting 0 views this week 0 watching⚡ Active
Interest: 44/100
44
Development Stage
✓
Pre-clinical✓
Phase 1✓
Phase 2✓
Phase 35
ApprovedIndication / Disease
Pyruvate Kinase Deficiency
Conditions
Pyruvate Kinase Deficiency, Anemia, Hemolytic
Trial Timeline
Jul 6, 2023 → Aug 1, 2029
NCT ID
NCT05777993About Mitapivat
Mitapivat is a approved stage product being developed by Agios Pharmaceuticals for Pyruvate Kinase Deficiency. The current trial status is recruiting. This product is registered under clinical trial identifier NCT05777993. Target conditions include Pyruvate Kinase Deficiency, Anemia, Hemolytic.
What happened to similar drugs?
0 of 5 similar drugs in Pyruvate Kinase Deficiency were approved
Approved (0) Terminated (0) Active (5)
Hype Score Breakdown
Clinical
20
Activity
15
Company
9
Novelty
0
Community
0
Clinical Trials (6)
| NCT ID | Phase | Status |
|---|---|---|
| NCT06286046 | Phase 2 | Recruiting |
| NCT07055243 | Phase 2 | Recruiting |
| NCT05777993 | Approved | Recruiting |
| NCT05610657 | Phase 1 | Completed |
| NCT05031780 | Phase 2/3 | Active |
| NCT03853798 | Phase 3 | Completed |
Competing Products
9 competing products in Pyruvate Kinase Deficiency
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| Triheptanoin | Ultragenyx Pharmaceutical | Phase 1 | 30 |
| Mitapivat + Mitapivat-matching placebo | Agios Pharmaceuticals | Phase 3 | 38 |
| Mitapivat + Mitapivat-matching placebo | Agios Pharmaceuticals | Phase 3 | 38 |
| Mitapivat | Agios Pharmaceuticals | Phase 3 | 34 |
| Placebo + AG-348 | Agios Pharmaceuticals | Phase 3 | 34 |
| AG-348 | Agios Pharmaceuticals | Phase 3 | 34 |
| AG-348 | Agios Pharmaceuticals | Phase 2 | 29 |
| RP-L301 | Rocket Pharmaceuticals | Phase 1 | 19 |
| RP-L301 | Rocket Pharmaceuticals | Phase 2 | 32 |