BMN 349 + Placebo

Phase 1Recruiting
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30
Hype Score

Development Stage

โœ“
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Alpha 1-Antitrypsin Deficiency

Conditions

Alpha 1-Antitrypsin Deficiency

Trial Timeline

Feb 21, 2025 โ†’ Sep 1, 2025

About BMN 349 + Placebo

BMN 349 + Placebo is a phase 1 stage product being developed by BioMarin Pharmaceutical for Alpha 1-Antitrypsin Deficiency. The current trial status is recruiting. This product is registered under clinical trial identifier NCT06738017. Target conditions include Alpha 1-Antitrypsin Deficiency.

Hype Score Breakdown

Clinical
10
Activity
5
Company
7
Novelty
3
Community
2

Clinical Trials (1)

NCT IDPhaseStatus
NCT06738017Phase 1Recruiting

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