VX-864

Phase 2Terminated
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51
Hype Score

Development Stage

Pre-clinical
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Alpha-1 Antitrypsin Deficiency

Conditions

Alpha-1 Antitrypsin Deficiency

Trial Timeline

Feb 23, 2023 → Aug 19, 2024

About VX-864

VX-864 is a phase 2 stage product being developed by Vertex Pharmaceuticals for Alpha-1 Antitrypsin Deficiency. The current trial status is terminated. This product is registered under clinical trial identifier NCT05643495. Target conditions include Alpha-1 Antitrypsin Deficiency.

Hype Score Breakdown

Clinical
17
Activity
12
Company
9
Novelty
5
Community
5

Clinical Trials (1)

NCT IDPhaseStatus
NCT05643495Phase 2Terminated

Competing Products

13 competing products in Alpha-1 Antitrypsin Deficiency

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49
Alpha-1 MPGrifolsPhase 3
74
Alpha-1 MPGrifolsPhase 3
74
WVE-006WaVe Life SciencesPhase 1
28
WVE-006WaVe Life SciencesPhase 1/2
36
INBRX-101/rhAAT-FcInhibrx BiosciencesPhase 1
28
Kamada-AAT for Inhalation, 80mg + Placebo + Kamada-AAT for Inhalation, 160mgKamadaPhase 2
44
KRRO-110Korro BioPhase 1/2
33
Alvelestat (MPH966)Mereo BioPharmaPhase 2
44