PA
Therapeutic Areas
Nippon Shinyaku Pipeline
| Drug | Indication | Phase |
|---|---|---|
| Viltolarsen (Viltepso) | Duchenne Muscular Dystrophy (Exon 53) | Approved |
| NS-089/NCNP-02 | Duchenne Muscular Dystrophy (Exon 44) | Phase 1/2 |
| Lusutrombopag (Mulpleta) | Thrombocytopenia in chronic liver disease | Approved |
| Fostamatinib (TAVALISSE) | Chronic Immune Thrombocytopenia (ITP) | Approved |
| NS-580/NM-8074 | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Phase 2 |