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Viltolarsen (Viltepso)

Duchenne Muscular Dystrophy (Exon 53)

ApprovedCommercial

Key Facts

Indication
Duchenne Muscular Dystrophy (Exon 53)
Phase
Approved
Status
Commercial
Company

About Nippon Shinyaku

Nippon Shinyaku's mission is to address high-unmet medical needs through pioneering science, particularly in rare diseases. Its key achievement is the development and commercialization of Viltepso (viltolarsen), an exon-skipping therapy for Duchenne muscular dystrophy, establishing its technological credibility. The company's strategy is built on deep R&D in targeted therapeutic areas, a dominant position in the Japanese market, and strategic international expansion, especially in the United States.

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Other Duchenne Muscular Dystrophy (Exon 53) Drugs

DrugCompanyPhase
WVE-N531WaVe Life SciencesPhase 1