KR

Keith Ryan

Director of Regulatory Affairs

Asklepion Pharmaceuticals

Asklepion Pharmaceuticals Pipeline

DrugIndicationPhase
IV L-citrullinePrevention of Sequelae of Acute Lung Injury in Pediatrics Undergoing Cardiopulmonary Bypass for Congenital Heart DefectsPhase 3
Cholbam (cholic acid)Bile Acid Synthesis Defects (e.g., peroxisomal disorders including Zellweger spectrum disorders)Approved