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IV L-citrulline

Prevention of Sequelae of Acute Lung Injury in Pediatrics Undergoing Cardiopulmonary Bypass for Congenital Heart Defects

Phase 3Active, enrollment concluded for Phase 3 trial

Key Facts

Indication
Prevention of Sequelae of Acute Lung Injury in Pediatrics Undergoing Cardiopulmonary Bypass for Congenital Heart Defects
Phase
Phase 3
Status
Active, enrollment concluded for Phase 3 trial
Company

About Asklepion Pharmaceuticals

Asklepion Pharmaceuticals is a mission-driven biotech dedicated to addressing the unmet medical needs of children with rare and critical diseases. Founded in 2006, the company leverages partnerships and a focused pipeline to advance therapies from concept to commercialization. Key achievements include an FDA-approved product (Cholbam), Orphan Drug Designation for its lead candidate, a Special Protocol Assessment (SPA) with the FDA for its Phase 3 program, and recognition from the National Organization for Rare Disorders (NORD). Its strategic direction centers on advancing IV citrulline through late-stage trials for a severe pediatric complication.

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