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David (Dave) Hava, Ph.D.

Chief Scientific Officer

Alltrna

Alltrna Pipeline

DrugIndicationPhase
AP003Arg-TGA (Arginine to TGA) Liver Stop Codon Disease (e.g., Methylmalonic Acidemia, Phenylketonuria, Organic Acidemias, Urea Cycle Disorders)Pre-clinical
Gln-TAG ProgramGln-TAG (Glutamine to TAG) Liver Stop Codon Disease (e.g., Phenylketonuria, Organic Acidemias, Urea Cycle Disorders)Discovery
Future Liver ProgramsOther nonsense mutations causing Liver Stop Codon DiseaseDiscovery