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Adrian Quartel, M.D., FFPM

Chief Medical Officer

Zevra Therapeutics

Zevra Therapeutics Pipeline

DrugIndicationPhase
Arimoclomol (MIPLYFFA)Niemann-Pick disease type C (NPC)Marketed
ArimoclomolNiemann-Pick disease type C (NPC)Filed
CeliprololVascular Ehlers-Danlos Syndrome (VEDS) - COL3A1 positivePhase 3
Sodium Phenylbutyrate (OLPRUVA)Urea Cycle Disorders (UCDs)Marketed