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Sodium Phenylbutyrate (OLPRUVA)

Urea Cycle Disorders (UCDs)

MarketedCommercially Available

Key Facts

Indication
Urea Cycle Disorders (UCDs)
Phase
Marketed
Status
Commercially Available
Company

About Zevra Therapeutics

Zevra Therapeutics is a mission-driven, commercial-stage biopharma company focused on rare diseases. Its strategy centers on acquiring and in-licensing promising candidates, then efficiently advancing them through clinical development and regulatory approval using a data-centric approach. The company has successfully transitioned to a commercial entity with two marketed products (MIPLYFFA® and OLPRUVA®) and maintains a late-stage pipeline with significant catalysts, including a Phase 3 trial for celiprolol in VEDS and a filed MAA for arimoclomol in NPC in Europe.

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