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TSRA-196

Alpha-1 Antitrypsin Deficiency (AATD)

Phase 1Active

Key Facts

Indication
Alpha-1 Antitrypsin Deficiency (AATD)
Phase
Phase 1
Status
Active
Company

About Tessera Therapeutics

Tessera Therapeutics is a Flagship Pioneering-incubated biotech developing a proprietary 'Gene Writing' platform, which it positions as a new category of genetic medicine beyond traditional gene editing and therapy. The technology is designed to make both small and large, permanent genomic alterations and is coupled with a non-viral delivery system. The company has advanced its lead in vivo program, TSRA-196 for Alpha-1 Antitrypsin Deficiency (AATD), into clinical development, with FDA Fast Track and Orphan Drug designations, and is also pursuing an HIV cure with grant support. As a private, pre-revenue company, Tessera is focused on translating its platform into potentially curative therapies for major unmet medical needs.

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Other Alpha-1 Antitrypsin Deficiency (AATD) Drugs

DrugCompanyPhase
Unnamed AATD ProgramAlveoGenePre-clinical
NB-101Nerai BiosciencesPre-clinical
UndisclosedGondolaBioIND Enabling
BEAM-302 (for Beam Therapeutics)Richmond PharmacologyPhase 1/2
KB408Krystal BiotechPreclinical
Alpha-1 Antitrypsin (AAT)GrifolsMarketed
BEAM-302Beam TherapeuticsPhase 1/2
GalNAc ProgramKorro BioPreclinical