Alpha-1 Antitrypsin (AAT)
Alpha-1 Antitrypsin Deficiency (AATD)
MarketedLifecycle Management
Key Facts
Indication
Alpha-1 Antitrypsin Deficiency (AATD)
Phase
Marketed
Status
Lifecycle Management
Company
About Grifols
Grifols is a century-old global leader in plasma-derived medicines and diagnostics, operating across four core divisions: Biopharma, Diagnostics, Bio Supplies, and Hospital Healthcare Solutions. Its mission to improve health is powered by deep plasma science expertise, a robust manufacturing footprint, and significant industry recognition, including repeated honors from TIME and Forbes. The company's strategy focuses on vertical integration in plasma, geographic expansion, and scientific innovation, including exploring new therapeutic areas like neurology through its CHRONOS-PD platform.
View full company profileTherapeutic Areas
Other Alpha-1 Antitrypsin Deficiency (AATD) Drugs
| Drug | Company | Phase |
|---|---|---|
| Unnamed AATD Program | AlveoGene | Pre-clinical |
| NB-101 | Nerai Biosciences | Pre-clinical |
| Undisclosed | GondolaBio | IND Enabling |
| TSRA-196 | Tessera Therapeutics | Phase 1 |
| BEAM-302 (for Beam Therapeutics) | Richmond Pharmacology | Phase 1/2 |
| KB408 | Krystal Biotech | Preclinical |
| BEAM-302 | Beam Therapeutics | Phase 1/2 |
| GalNAc Program | Korro Bio | Preclinical |