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Alpha-1 Antitrypsin (AAT)

Alpha-1 Antitrypsin Deficiency (AATD)

MarketedLifecycle Management

Key Facts

Indication
Alpha-1 Antitrypsin Deficiency (AATD)
Phase
Marketed
Status
Lifecycle Management
Company

About Grifols

Grifols is a century-old global leader in plasma-derived medicines and diagnostics, operating across four core divisions: Biopharma, Diagnostics, Bio Supplies, and Hospital Healthcare Solutions. Its mission to improve health is powered by deep plasma science expertise, a robust manufacturing footprint, and significant industry recognition, including repeated honors from TIME and Forbes. The company's strategy focuses on vertical integration in plasma, geographic expansion, and scientific innovation, including exploring new therapeutic areas like neurology through its CHRONOS-PD platform.

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Other Alpha-1 Antitrypsin Deficiency (AATD) Drugs

DrugCompanyPhase
Unnamed AATD ProgramAlveoGenePre-clinical
NB-101Nerai BiosciencesPre-clinical
UndisclosedGondolaBioIND Enabling
TSRA-196Tessera TherapeuticsPhase 1
BEAM-302 (for Beam Therapeutics)Richmond PharmacologyPhase 1/2
KB408Krystal BiotechPreclinical
BEAM-302Beam TherapeuticsPhase 1/2
GalNAc ProgramKorro BioPreclinical