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Sarizotan

Rett Syndrome

Phase IIIDiscontinued

Key Facts

Indication
Rett Syndrome
Phase
Phase III
Status
Discontinued
Company

About Newron Pharmaceuticals

Newron Pharmaceuticals is a development-stage biopharma focused on novel therapies for neurological diseases. Its primary achievement is the global approval and commercialization of Xadago® for Parkinson's disease, providing a revenue foundation. The company's strategy centers on advancing a pipeline of innovative small molecules for rare CNS disorders, leveraging strategic partnerships to maximize reach while retaining key rights. With a lean operational model, Newron aims to address significant unmet medical needs in neuroscience.

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Therapeutic Areas

Other Rett Syndrome Drugs

DrugCompanyPhase
NTI164Neurotech InternationalPhase 2
RTT1Grann PharmaceuticalsPre-clinical
NEX-1 / NEX-2Nexien BioPharmaPre-clinical / Phase 1
KIT-13NeuroCoresPre-clinical
DPM-1003DepYmedPhase 1
ExoEdit® for Rett SyndromeEvox TherapeuticsPre-clinical
RVL-001 (vorinostat)Unravel BiosciencesClinical Trial Initiated
Rett Syndrome ProgramHerophilusDiscovery
Glutamate Modulator for Rett SyndromeNumedicusLicensed/Orphan Designation
TTI-0102Thiogenesis TherapeuticsPhase 1
DAYBUE® (trofinetide)Neuren PharmaceuticalsApproved
TSHA-102Taysha Gene TherapiesPhase 1/2