Home/Pipeline/ExoEdit® for Rett Syndrome

ExoEdit® for Rett Syndrome

Rett Syndrome

Pre-clinicalActive

Key Facts

Indication
Rett Syndrome
Phase
Pre-clinical
Status
Active
Company

About Evox Therapeutics

Evox Therapeutics is a private, pre-clinical stage biotech founded in 2016 and headquartered in Oxford, UK. The company is developing a novel therapeutic platform, ExoEdit®, which leverages engineered exosomes to deliver proprietary gene editors to the brain, aiming to address the root cause of genetically-driven neurodegenerative diseases. Its strategy involves building a pipeline based on human genetic data and preclinical validation while actively seeking strategic partnerships to advance its mission. Recent activities include a collaboration with the Rett Syndrome Research Trust and strengthening its governance with key board and advisory appointments.

View full company profile

Other Rett Syndrome Drugs

DrugCompanyPhase
RTT1Grann PharmaceuticalsPre-clinical
NEX-1 / NEX-2Nexien BioPharmaPre-clinical / Phase 1
KIT-13NeuroCoresPre-clinical
DPM-1003DepYmedPhase 1
RVL-001 (vorinostat)Unravel BiosciencesClinical Trial Initiated
Rett Syndrome ProgramHerophilusDiscovery
Glutamate Modulator for Rett SyndromeNumedicusLicensed/Orphan Designation
DAYBUE® (trofinetide)Neuren PharmaceuticalsApproved
TSHA-102Taysha Gene TherapiesPhase 1/2
SarizotanNewron PharmaceuticalsPhase III
NGN-401NeurogenePhase 1/2 & Registrational
Blarcamesine (ANAVEX®2-73)Anavex Life SciencesPhase 2/3