HLX-0553
Angelman Syndrome
PreclinicalActive
Key Facts
About Healx
Healx is a private, clinical-stage biotech applying a proprietary AI platform to transform drug discovery for rare diseases, an area traditionally neglected due to high costs and low success rates. The company has built a pipeline with programs ranging from preclinical to Phase 2, primarily in rare neurology and oncology, and actively partners with patient groups and academic consortia. By using technology to identify novel drug-disease relationships and repurpose known compounds, Healx aims to run multiple programs in parallel, increasing the speed and probability of delivering treatments to patients.
View full company profileTherapeutic Areas
Other Angelman Syndrome Drugs
| Drug | Company | Phase |
|---|---|---|
| Undisclosed Pipeline Programs | AS2 Bio | Pre-clinical |
| Rugonersen (OHB-724) | Oak Hill Bio | Phase 3 |
| GTX-102 | Ultragenyx Pharmaceutical | Phase 1/2 |
| NNZ-2591 | Neuren Pharmaceuticals | Phase 2 |