Home/Pipeline/Undisclosed Pipeline Programs

Undisclosed Pipeline Programs

Angelman syndrome

Pre-clinicalActive

Key Facts

Indication
Angelman syndrome
Phase
Pre-clinical
Status
Active
Company

About AS2 Bio

AS2 Bio is a private, pre-clinical stage biotech dedicated to creating therapies for Angelman syndrome (AS), a rare neurodevelopmental disorder. The company is building a pipeline across multiple therapeutic modalities, including targeted protein degradation, and is led by a team with deep experience in rare disease drug development and direct personal connections to the AS community. Its strategy is closely tied to the Foundation for Angelman Syndrome Therapeutics (FAST), leveraging established research consortia and regulatory pathways to advance its programs.

View full company profile

Other Angelman syndrome Drugs

DrugCompanyPhase
HLX-0553HealxPreclinical
Rugonersen (OHB-724)Oak Hill BioPhase 3
GTX-102Ultragenyx PharmaceuticalPhase 1/2
NNZ-2591Neuren PharmaceuticalsPhase 2