Pegvaliase-Pqpz

Pre-clinicalCompleted
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20
Hype Score

Development Stage

1
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Phenylketonurias

Conditions

Phenylketonurias

Trial Timeline

May 25, 2022 โ†’ Jul 1, 2025

About Pegvaliase-Pqpz

Pegvaliase-Pqpz is a pre-clinical stage product being developed by BioMarin Pharmaceutical for Phenylketonurias. The current trial status is completed. This product is registered under clinical trial identifier NCT05356377. Target conditions include Phenylketonurias.

Hype Score Breakdown

Clinical
5
Activity
2
Company
7
Novelty
2
Community
1

Clinical Trials (1)

NCT IDPhaseStatus
NCT05356377Pre-clinicalCompleted

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PalynziqBioMarin PharmaceuticalPre-clinical
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