Pegvaliase-Pqpz
Pre-clinicalCompleted 0 views this week 0 watching💤 Quiet
Interest: 23/100
23
Development Stage
1
Pre-clinical2
Phase 13
Phase 24
Phase 35
ApprovedIndication / Disease
Phenylketonurias
Conditions
Phenylketonurias
Trial Timeline
May 25, 2022 → Jul 1, 2025
NCT ID
NCT05356377About Pegvaliase-Pqpz
Pegvaliase-Pqpz is a pre-clinical stage product being developed by BioMarin Pharmaceutical for Phenylketonurias. The current trial status is completed. This product is registered under clinical trial identifier NCT05356377. Target conditions include Phenylketonurias.
What happened to similar drugs?
0 of 3 similar drugs in Phenylketonurias were approved
Approved (0) Terminated (0) Active (3)
Hype Score Breakdown
Clinical
3
Activity
8
Company
12
Novelty
0
Community
0
Clinical Trials (1)
| NCT ID | Phase | Status |
|---|---|---|
| NCT05356377 | Pre-clinical | Completed |
Competing Products
7 competing products in Phenylketonurias
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| Sapropterin | BioMarin Pharmaceutical | Pre-clinical | 23 |
| Pegvaliase | BioMarin Pharmaceutical | Pre-clinical | 23 |
| sapropterin dihydrochloride | BioMarin Pharmaceutical | Phase 2 | 32 |
| sapropterin dihydrochloride | BioMarin Pharmaceutical | Phase 3 | 37 |
| sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin | BioMarin Pharmaceutical | Phase 3 | 37 |
| Palynziq | BioMarin Pharmaceutical | Pre-clinical | 30 |
| Sapropterin Dihydrochloride + Placebo | BioMarin Pharmaceutical | Phase 3 | 37 |