Palynziq

Pre-clinicalRecruiting
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20
Hype Score

Development Stage

1
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Phenylketonurias

Conditions

Phenylketonurias

Trial Timeline

Oct 8, 2019 โ†’ Dec 1, 2028

About Palynziq

Palynziq is a pre-clinical stage product being developed by BioMarin Pharmaceutical for Phenylketonurias. The current trial status is recruiting. This product is registered under clinical trial identifier NCT04404530. Target conditions include Phenylketonurias.

Hype Score Breakdown

Clinical
5
Activity
2
Company
7
Novelty
2
Community
1

Clinical Trials (1)

NCT IDPhaseStatus
NCT04404530Pre-clinicalRecruiting

Competing Products

7 competing products in Phenylketonurias

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SapropterinBioMarin PharmaceuticalPre-clinical
20
PegvaliaseBioMarin PharmaceuticalPre-clinical
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sapropterin dihydrochlorideBioMarin PharmaceuticalPhase 2
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sapropterin dihydrochlorideBioMarin PharmaceuticalPhase 3
74
sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterinBioMarin PharmaceuticalPhase 3
74
Pegvaliase-PqpzBioMarin PharmaceuticalPre-clinical
20
Sapropterin Dihydrochloride + PlaceboBioMarin PharmaceuticalPhase 3
74