Patisiran
Pre-clinicalCompleted 0 watching 0 views this week๐ค Quiet
20
Development Stage
1
Pre-clinical2
Phase 13
Phase 24
Phase 35
ApprovedIndication / Disease
Transthyretin-mediated Amyloidosis With Cardiomyopathy
Conditions
Transthyretin-mediated Amyloidosis With Cardiomyopathy, ATTR Amyloidosis With Cardiomyopathy
Trial Timeline
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NCT ID
NCT05505838About Patisiran
Patisiran is a pre-clinical stage product being developed by Alnylam Pharmaceuticals for Transthyretin-mediated Amyloidosis With Cardiomyopathy. The current trial status is completed. This product is registered under clinical trial identifier NCT05505838. Target conditions include Transthyretin-mediated Amyloidosis With Cardiomyopathy, ATTR Amyloidosis With Cardiomyopathy.
Hype Score Breakdown
Clinical
5
Activity
2
Company
7
Novelty
2
Community
1
Clinical Trials (6)
| NCT ID | Phase | Status |
|---|---|---|
| NCT05505838 | Pre-clinical | Completed |
| NCT05023889 | Phase 1 | Active |
| NCT04201418 | Pre-clinical | Completed |
| NCT03862807 | Phase 3 | Completed |
| NCT02510261 | Phase 3 | Completed |
| NCT01617967 | Phase 2 | Completed |
Competing Products
9 competing products in Transthyretin-mediated Amyloidosis With Cardiomyopathy
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| Eplontersen Solution for Injection | AstraZeneca | Phase 1 | 33 |
| Eplontersen + Placebo | AstraZeneca | Phase 3 | 77 |
| Eplontersen | AstraZeneca | Phase 3 | 77 |
| Patisiran | Alnylam Pharmaceuticals | Pre-clinical | 20 |
| ALN-TTRSC02 + Sterile Normal Saline (0.9% NaCl) | Alnylam Pharmaceuticals | Phase 1 | 30 |
| Nucresiran + Vutrisiran | Alnylam Pharmaceuticals | Phase 3 | 74 |
| ALN-TTRSC04 + Placebo | Alnylam Pharmaceuticals | Phase 1 | 30 |
| Eplontersen | Ionis Pharmaceuticals | Phase 3 | 74 |
| Inotersen + Eplontersen | Ionis Pharmaceuticals | Phase 3 | 74 |