ALN-TTRSC02 + Sterile Normal Saline (0.9% NaCl)

Phase 1Completed
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30
Hype Score

Development Stage

โœ“
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Transthyretin-mediated Amyloidosis (ATTR Amyloidosis)

Conditions

Transthyretin-mediated Amyloidosis (ATTR Amyloidosis)

Trial Timeline

Jun 7, 2016 โ†’ Jan 12, 2018

About ALN-TTRSC02 + Sterile Normal Saline (0.9% NaCl)

ALN-TTRSC02 + Sterile Normal Saline (0.9% NaCl) is a phase 1 stage product being developed by Alnylam Pharmaceuticals for Transthyretin-mediated Amyloidosis (ATTR Amyloidosis). The current trial status is completed. This product is registered under clinical trial identifier NCT02797847. Target conditions include Transthyretin-mediated Amyloidosis (ATTR Amyloidosis).

Hype Score Breakdown

Clinical
10
Activity
5
Company
7
Novelty
3
Community
2

Clinical Trials (1)

NCT IDPhaseStatus
NCT02797847Phase 1Completed

Competing Products

9 competing products in Transthyretin-mediated Amyloidosis (ATTR Amyloidosis)

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Eplontersen Solution for InjectionAstraZenecaPhase 1
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EplontersenAstraZenecaPhase 3
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PatisiranAlnylam PharmaceuticalsPre-clinical
20
PatisiranAlnylam PharmaceuticalsPre-clinical
20
Nucresiran + VutrisiranAlnylam PharmaceuticalsPhase 3
74
ALN-TTRSC04 + PlaceboAlnylam PharmaceuticalsPhase 1
30
EplontersenIonis PharmaceuticalsPhase 3
74
Inotersen + EplontersenIonis PharmaceuticalsPhase 3
74