IONIS-DMPKRx + Placebo
Phase 1/2Completed 0 watching 0 views this week💤 Quiet
38
Development Stage
✓
Pre-clinical2
Phase 13
Phase 24
Phase 35
ApprovedIndication / Disease
Myotonic Dystrophy Type 1
Conditions
Myotonic Dystrophy Type 1
Trial Timeline
Dec 1, 2014 → Aug 1, 2016
NCT ID
NCT02312011About IONIS-DMPKRx + Placebo
IONIS-DMPKRx + Placebo is a phase 1/2 stage product being developed by Ionis Pharmaceuticals for Myotonic Dystrophy Type 1. The current trial status is completed. This product is registered under clinical trial identifier NCT02312011. Target conditions include Myotonic Dystrophy Type 1.
Hype Score Breakdown
Clinical
13
Activity
8
Company
7
Novelty
4
Community
3
Clinical Trials (1)
| NCT ID | Phase | Status |
|---|---|---|
| NCT02312011 | Phase 1/2 | Completed |
Competing Products
16 competing products in Myotonic Dystrophy Type 1
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| Tideglusib | AMO Pharma | Pre-clinical | 15 |
| Tideglusib | AMO Pharma | Phase 2 | 44 |
| Tideglusib + Placebo | AMO Pharma | Phase 2/3 | 57 |
| Tideglusib | AMO Pharma | Phase 2/3 | 57 |
| VX-670 | Vertex Pharmaceuticals | Phase 2 | 51 |
| VX-670 + Placebo | Vertex Pharmaceuticals | Phase 1/2 | 40 |
| SAR446268 | Sanofi | Phase 1/2 | 40 |
| rhIGF-I/rhIGFBP-3 + placebo | Insmed | Phase 2 | 49 |
| Del-desiran (AOC 1001) | Avidity Biosciences | Phase 3 | 74 |
| ARO-DM1 Intravenous (IV) Infusion + Placebo Intravenous (IV) Infusion + ARO-DM1 subcutaneous (SC) injection + Placebo Subcutaneous (SC) Injection | Arrowhead Pharmaceuticals | Phase 1/2 | 38 |
| DYNE-101 + Placebo | Dyne Therapeutics | Phase 3 | 72 |
| DYNE-101 + Placebo | Dyne Therapeutics | Phase 1/2 | 36 |
| Pitolisant Oral Tablet + Placebo oral tablet | Harmony Biosciences | Phase 2 | 47 |
| PGN-EDODM1 | PepGen | Phase 2 | 44 |
| PGN-EDODM1 | PepGen | Phase 2 | 44 |
| PGN-EDODM1 for infusion | PepGen | Phase 1 | 25 |