Pitolisant Oral Tablet + Placebo oral tablet
Phase 2Completed 0 watching 0 views this week⚡ Active
47
Development Stage
✓
Pre-clinical✓
Phase 13
Phase 24
Phase 35
ApprovedIndication / Disease
Myotonic Dystrophy 1
Conditions
Myotonic Dystrophy 1, Excessive Daytime Sleepiness
Trial Timeline
Jun 28, 2021 → Oct 31, 2024
NCT ID
NCT04886518About Pitolisant Oral Tablet + Placebo oral tablet
Pitolisant Oral Tablet + Placebo oral tablet is a phase 2 stage product being developed by Harmony Biosciences for Myotonic Dystrophy 1. The current trial status is completed. This product is registered under clinical trial identifier NCT04886518. Target conditions include Myotonic Dystrophy 1, Excessive Daytime Sleepiness.
Hype Score Breakdown
Clinical
17
Activity
12
Company
5
Novelty
5
Community
5
Clinical Trials (1)
| NCT ID | Phase | Status |
|---|---|---|
| NCT04886518 | Phase 2 | Completed |
Competing Products
16 competing products in Myotonic Dystrophy 1
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| Tideglusib | AMO Pharma | Pre-clinical | 15 |
| Tideglusib | AMO Pharma | Phase 2 | 44 |
| Tideglusib + Placebo | AMO Pharma | Phase 2/3 | 57 |
| Tideglusib | AMO Pharma | Phase 2/3 | 57 |
| VX-670 | Vertex Pharmaceuticals | Phase 2 | 51 |
| VX-670 + Placebo | Vertex Pharmaceuticals | Phase 1/2 | 40 |
| SAR446268 | Sanofi | Phase 1/2 | 40 |
| rhIGF-I/rhIGFBP-3 + placebo | Insmed | Phase 2 | 49 |
| IONIS-DMPKRx + Placebo | Ionis Pharmaceuticals | Phase 1/2 | 38 |
| Del-desiran (AOC 1001) | Avidity Biosciences | Phase 3 | 74 |
| ARO-DM1 Intravenous (IV) Infusion + Placebo Intravenous (IV) Infusion + ARO-DM1 subcutaneous (SC) injection + Placebo Subcutaneous (SC) Injection | Arrowhead Pharmaceuticals | Phase 1/2 | 38 |
| DYNE-101 + Placebo | Dyne Therapeutics | Phase 3 | 72 |
| DYNE-101 + Placebo | Dyne Therapeutics | Phase 1/2 | 36 |
| PGN-EDODM1 | PepGen | Phase 2 | 44 |
| PGN-EDODM1 | PepGen | Phase 2 | 44 |
| PGN-EDODM1 for infusion | PepGen | Phase 1 | 25 |