CTX001
Phase 2/3Completed 0 watching 0 views this week📈 Rising
64
Development Stage
✓
Pre-clinical✓
Phase 13
Phase 24
Phase 35
ApprovedIndication / Disease
Beta-Thalassemia
Conditions
Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn, Hematologic Diseases, Hemoglobinopathies
Trial Timeline
Sep 14, 2018 → Nov 13, 2025
NCT ID
NCT03655678About CTX001
CTX001 is a phase 2/3 stage product being developed by Vertex Pharmaceuticals for Beta-Thalassemia. The current trial status is completed. This product is registered under clinical trial identifier NCT03655678. Target conditions include Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn.
Hype Score Breakdown
Clinical
22
Activity
15
Company
9
Novelty
7
Community
8
Clinical Trials (6)
| NCT ID | Phase | Status |
|---|---|---|
| NCT05477563 | Phase 3 | Recruiting |
| NCT05356195 | Phase 3 | Active |
| NCT05329649 | Phase 3 | Active |
| NCT04208529 | Phase 3 | Recruiting |
| NCT03745287 | Phase 2/3 | Completed |
| NCT03655678 | Phase 2/3 | Completed |
Competing Products
18 competing products in Beta-Thalassemia
| Product | Company | Stage | Hype Score |
|---|---|---|---|
| ACE-536 | Merck | Phase 2 | 52 |
| Deferasirox | Novartis | Approved | 85 |
| Zoledronic acid + Placebo | Novartis | Phase 2/3 | 65 |
| deferasirox | Novartis | Phase 3 | 77 |
| ICL670 + deferoxamine | Novartis | Phase 3 | 77 |
| Deferasirox | Novartis | Phase 2 | 52 |
| Deferasirox | Novartis | Phase 2 | 52 |
| ICL670 | Novartis | Approved | 85 |
| Bitopertin | Roche | Phase 2 | 52 |
| Luspatercept + Placebo | Bristol Myers Squibb | Phase 2 | 51 |
| CTX001 | Vertex Pharmaceuticals | Phase 3 | 76 |
| CTX001 | Vertex Pharmaceuticals | Phase 3 | 76 |
| CTX001 | Vertex Pharmaceuticals | Phase 3 | 76 |
| Mozobil + Mozobil + Mozobil | Sanofi | Pre-clinical | 22 |
| Deferitrin (GT56-252) + desferoxamine (DFO) | Sanofi | Phase 1/2 | 40 |
| REGN7999 + Placebo | Regeneron Pharmaceuticals | Phase 2 | 51 |
| VIT-2763 60 mg QD + VIT-2763 60 mg BID + VIT-2763 120 mg BID + Placebo | LabCorp | Phase 2 | 49 |
| VIT-2763 once a day (QD) + VIT-2763 twice a day (BID) + Placebo | LabCorp | Phase 2 | 49 |