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Timothy Miller

Strategic Advisor, Former President & CEO

ReGenX Biosciences

ReGenX Biosciences Pipeline

DrugIndicationPhase
RGX-314Wet Age-Related Macular Degeneration (wAMD)Phase II
RGX-121Mucopolysaccharidosis Type II (MPS II)Phase I/II
RGX-181CLN2 Disease (Batten Disease)Phase I/II
RGX-111Mucopolysaccharidosis Type I (MPS I)Phase I/II
RGX-381Ocular manifestations of Epidermolysis BullosaPhase I/II