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DS

Dr. Steve Pakola

Chief Medical Officer

REGENXBIO

REGENXBIO Pipeline

DrugIndicationPhase
RGX-314Wet Age-related Macular Degeneration (wAMD)Phase 2
RGX-202Duchenne Muscular Dystrophy (DMD)Phase 1/2
RGX-121Mucopolysaccharidosis Type II (MPS II, Hunter syndrome)Phase 1/2
RGX-181Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2 Disease)Preclinical
RGX-381Ocular manifestations of FA Deficiency (FAD)Phase 1/2
ABBV-RGX-314Wet AMD & Diabetic RetinopathyPhase 3