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Susan Slaugenhaupt, PhD

Scientific Director (Collaborator)

Tikun Therapeutics

Tikun Therapeutics Pipeline

DrugIndicationPhase
Next-Generation ELP1 Splicing CorrectorsFamilial Dysautonomia (FD)Pre-clinical
ELP1 Gene Replacement TherapyFamilial Dysautonomia with optic neuropathyPre-clinical