EM
Therapeutic Areas
Tikun Therapeutics Pipeline
| Drug | Indication | Phase |
|---|---|---|
| Next-Generation ELP1 Splicing Correctors | Familial Dysautonomia (FD) | Pre-clinical |
| ELP1 Gene Replacement Therapy | Familial Dysautonomia with optic neuropathy | Pre-clinical |
| Drug | Indication | Phase |
|---|---|---|
| Next-Generation ELP1 Splicing Correctors | Familial Dysautonomia (FD) | Pre-clinical |
| ELP1 Gene Replacement Therapy | Familial Dysautonomia with optic neuropathy | Pre-clinical |