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Shuli Kulak, M.D.

Head of Corporate Strategy and Business Development

Solid Biosciences

Solid Biosciences Pipeline

DrugIndicationPhase
SGT-003Duchenne Muscular Dystrophy (Duchenne)Phase I/II
SGT-212Friedreich’s ataxia (FA)Phase I/II
SGT-501Catecholaminergic polymorphic ventricular tachycardia (CPVT)Phase I/II
SGT-601TNNT2-mediated dilated cardiomyopathy and additional fatal, genetic cardiac diseasesPreclinical