SGT-601
TNNT2-mediated dilated cardiomyopathy and additional fatal, genetic cardiac diseases
PreclinicalActive
Key Facts
Indication
TNNT2-mediated dilated cardiomyopathy and additional fatal, genetic cardiac diseases
Phase
Preclinical
Status
Active
Company
About Solid Biosciences
Solid Biosciences is a publicly traded biotech focused on advancing a portfolio of gene therapy candidates for rare neuromuscular and cardiac diseases, including lead program SGT-003 for Duchenne muscular dystrophy. The company's strategy is dual-pronged: progressing specific therapeutic candidates through clinical development while investing in proprietary platform technologies, such as libraries of genetic regulators, to enhance gene therapy delivery and efficacy broadly. With a founding story rooted in personal patient experience, Solid aims to improve daily life outcomes by uniting expertise in science, technology, and disease management.
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