SM
Therapeutic Areas
Nerai Biosciences Pipeline
| Drug | Indication | Phase |
|---|---|---|
| NB-301 | Citrullinemia type 1 (CTLN1) | Pre-clinical |
| NB-20X | Phenylketonuria (PKU) | Pre-clinical |
| NB-101 | Alpha-1 antitrypsin deficiency (AATD) | Pre-clinical |
| NB-401 | Homocystinuria | Discovery |
| NB-701 | Undisclosed | Discovery |
| NB-501 | Classical galactosemia type 1 | Discovery |
| NB-601 | Primary hyperoxaluria | Discovery |
| NB-e101 | Autosomal Dominant Retinitis Pigmentosa (adRP) | Discovery |