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KM

Kim Marquart

Scientific Co-founder

Nerai Biosciences

Nerai Biosciences Pipeline

DrugIndicationPhase
NB-301Citrullinemia type 1 (CTLN1)Pre-clinical
NB-20XPhenylketonuria (PKU)Pre-clinical
NB-101Alpha-1 antitrypsin deficiency (AATD)Pre-clinical
NB-401HomocystinuriaDiscovery
NB-701UndisclosedDiscovery
NB-501Classical galactosemia type 1Discovery
NB-601Primary hyperoxaluriaDiscovery
NB-e101Autosomal Dominant Retinitis Pigmentosa (adRP)Discovery