PS

Phillip Sharp

Co-Founder & Director

Alnylam Pharmaceuticals

Alnylam Pharmaceuticals Pipeline

DrugIndicationPhase
AMVUTTRA (vutrisiran)hATTR Amyloidosis with PolyneuropathyApproved
ONPATTRO (patisiran)hATTR Amyloidosis with PolyneuropathyApproved
GIVLAARI (givosiran)Acute Hepatic Porphyria (AHP)Approved
OXLUMO (lumasiran)Primary Hyperoxaluria Type 1 (PH1)Approved
LEQVIO (inclisiran)HypercholesterolemiaApproved
Zilebesiran (ALN-AGT)HypertensionPhase 3
ALN-APPAlzheimer's Disease, Cerebral Amyloid AngiopathyPhase 2
Fitusiran (ALN-AT3SC)Hemophilia A and BPhase 3