JM

John Maraganore

Founding CEO, Executive Chairman of the Board

Alnylam Pharmaceuticals

Alnylam Pharmaceuticals Pipeline

DrugIndicationPhase
AMVUTTRA (vutrisiran)hATTR Amyloidosis with PolyneuropathyApproved
ONPATTRO (patisiran)hATTR Amyloidosis with PolyneuropathyApproved
GIVLAARI (givosiran)Acute Hepatic Porphyria (AHP)Approved
OXLUMO (lumasiran)Primary Hyperoxaluria Type 1 (PH1)Approved
LEQVIO (inclisiran)HypercholesterolemiaApproved
Zilebesiran (ALN-AGT)HypertensionPhase 3
ALN-APPAlzheimer's Disease, Cerebral Amyloid AngiopathyPhase 2
Fitusiran (ALN-AT3SC)Hemophilia A and BPhase 3