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JA

John A. Kelly, Ph.D.

Chief Scientific Officer & SVP, Research

Precision BioSciences

Precision BioSciences Pipeline

DrugIndicationPhase
PBGENE-HBVChronic Hepatitis B Virus (HBV) InfectionPhase 1/2
PBGENE-DMDDuchenne Muscular Dystrophy (DMD)Phase 1/2
PBGENE-PMMPrimary Mitochondrial Myopathy (PMM)Preclinical
Azer-celB-cell Malignancies / Autoimmune DiseasesPhase 1/2
ECUR-506Ornithine Transcarbamylase (OTC) DeficiencyPhase 1/2